- Two kids with adrenoleukodystrophy, were treated, and their disease has been arrested for two years. They tried this experimental method because they couldn't find any matching blood-marrow donors.
- Five kids and seven adults blind from a rare congenital eye disease, had their sight partially restored.
- "8 out of 10 patients with a rare immunological disorder were cured"
Friday, November 6, 2009
NY Times article about recent small successes in gene therapy.