Friday, November 6, 2009

Gene therapy successes

NY Times article about recent small successes in gene therapy.
  • Two kids with adrenoleukodystrophy, were treated, and their disease has been arrested for two years. They tried this experimental method because they couldn't find any matching blood-marrow donors. 
  • Five kids and seven adults blind from a rare congenital eye disease, had their sight partially restored.
  • "8 out of 10 patients with a rare immunological disorder were cured"
When they first tried this kind of therapy, they used a modified mouse leukemia virus to insert the genes into the kids' DNA, and some of the kids they tried it on got leukemia and died, but they've found a new way to  insert the genes.

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